{"id":528,"date":"2023-06-15T22:05:00","date_gmt":"2023-06-15T20:05:00","guid":{"rendered":"https:\/\/onlyproject.org\/beginning-of-a-phase-1-clinical-trial-what-to-expect\/"},"modified":"2023-07-21T18:55:14","modified_gmt":"2023-07-21T16:55:14","slug":"beginning-of-a-phase-1-clinical-trial-what-to-expect","status":"publish","type":"post","link":"https:\/\/onlyproject.org\/fr\/beginning-of-a-phase-1-clinical-trial-what-to-expect\/","title":{"rendered":"D\u00e9but de l&rsquo;essai clinique de phase 1 : \u00e0 quoi s&rsquo;attendre ?"},"content":{"rendered":"\r\n<section id=\"ac-block_04dea93798658f22e37c37dbc18e7739\" class=\"block-content-title\">\r\n    \r\n    <h2 class=\"title\"><p>Ces derni\u00e8res ann\u00e9es, une partie importante des fonds d&rsquo;Only Watch a \u00e9t\u00e9 mobilis\u00e9e pour mettre en place un essai clinique pour une th\u00e9rapie d\u00e9velopp\u00e9e par une biotech cr\u00e9\u00e9e avec un consortium de parents et de chercheurs\u00b7euses et dont l&rsquo;AMM est le principal bailleur de fonds.<\/p>\n<\/h2>\r\n    \r\n<\/section>\n\n\r\n<section id=\"ac-block_e10239133451d8fc2f5e85293b2ed6e3\" class=\"block-content-text has-wysiwyg-content\">\r\n    \r\n    <p>Le m\u00e9dicament d\u00e9velopp\u00e9 s&rsquo;appelle SQY51 et vise \u00e0 traiter les patients atteints d&rsquo;une d\u00e9l\u00e9tion sur l&rsquo;exon (unit\u00e9 de coupe du g\u00e8ne) num\u00e9ro 51.<\/p>\n    \r\n<\/section>\n\n\r\n<section id=\"ac-block_c25b6be5edcc59f306b90bd8e7015565\" class=\"block-content-title-separator style-normal\">\r\n    \r\n    <div class=\"title-container title-bar-style\">\r\n\r\n                    \r\n            <h2 class=\"title\">A quoi s&rsquo;attendre ?<\/h2>\r\n\r\n        \r\n    <\/div>\r\n    \r\n\r\n            <p>Si l&rsquo;essai est concluant, il pourrait conduire \u00e0 d&rsquo;autres essais pour d&rsquo;autres exons et d&rsquo;autres maladies. En effet, le g\u00e8ne de la dystrophine \u00e9tant l&rsquo;un des plus longs de l&rsquo;ADN, il repr\u00e9sente un excellent cas d&rsquo;\u00e9tude et les solutions actuellement test\u00e9es pourraient avoir de nombreuses applications pour de nombreuses maladies g\u00e9n\u00e9tiques.<\/p>\n<p>Si, malgr\u00e9 tous les efforts d\u00e9ploy\u00e9s pour assurer la s\u00e9curit\u00e9 et l&rsquo;efficacit\u00e9, ce premier essai n&rsquo;\u00e9tait pas concluant, le processus serait relanc\u00e9 au niveau de la recherche en laboratoire dans le but de lancer un deuxi\u00e8me essai. Bien que ce sc\u00e9nario ne soit pas enthousiasmant, l&rsquo;association l&rsquo;envisage afin de pouvoir soutenir le projet \u00e0 long terme.<\/p>\n<p>La technologie d\u00e9velopp\u00e9e \u00e9tant tr\u00e8s prometteuse, des partenariats ont d\u00e9j\u00e0 \u00e9t\u00e9 scell\u00e9s pour tester la technologie sur d&rsquo;autres maladies comme l&rsquo;\u00e9pidermolyse bulleuse ou l&rsquo;amyotrophie spinale.<\/p>\n    \r\n    \r\n<\/section>\n\n\r\n<section id=\"ac-block_c8601873a7813bca78399b6ba4790509\" class=\"block-content-title-separator style-normal\">\r\n    \r\n    <div class=\"title-container title-bar-style\">\r\n\r\n                    \r\n            <h2 class=\"title\">\ud83c\udfa5 En savoir plus sur l&rsquo;essai clinique en pr\u00e9paration<\/h2>\r\n\r\n        \r\n    <\/div>\r\n    \r\n\r\n    \r\n    \r\n<\/section>\n\n\r\n<section id=\"ac-block_cfcaa87356db3eae71f9cbc11f1ff0a5\" class=\"block-content-text has-wysiwyg-content\">\r\n    \r\n    <p><a href=\"https:\/\/youtu.be\/EdZscEvYNoE\"><span style=\"font-weight: 400;\">Echange sur la recherche sur la myopathie de Duchenne et les essais cliniques \u00e0 venir<\/span><\/a><\/p>\n    \r\n<\/section>","protected":false},"excerpt":{"rendered":"","protected":false},"author":1,"featured_media":517,"comment_status":"open","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"_acf_changed":false,"footnotes":""},"categories":[9],"tags":[],"class_list":["post-528","post","type-post","status-publish","format-standard","has-post-thumbnail","hentry","category-non-classifiee"],"acf":[],"yoast_head":"<!-- This site is optimized with the Yoast SEO plugin v27.4 - https:\/\/yoast.com\/product\/yoast-seo-wordpress\/ -->\n<title>D\u00e9but de l&#039;essai clinique de phase 1 : \u00e0 quoi s&#039;attendre ? - ONLY Project<\/title>\n<meta name=\"robots\" content=\"index, follow, max-snippet:-1, max-image-preview:large, max-video-preview:-1\" \/>\n<link rel=\"canonical\" href=\"https:\/\/onlyproject.org\/fr\/beginning-of-a-phase-1-clinical-trial-what-to-expect\/\" \/>\n<meta property=\"og:locale\" content=\"fr_FR\" \/>\n<meta property=\"og:type\" content=\"article\" \/>\n<meta property=\"og:title\" content=\"D\u00e9but de l&#039;essai clinique de phase 1 : \u00e0 quoi s&#039;attendre ? - ONLY Project\" \/>\n<meta property=\"og:url\" content=\"https:\/\/onlyproject.org\/fr\/beginning-of-a-phase-1-clinical-trial-what-to-expect\/\" \/>\n<meta property=\"og:site_name\" content=\"ONLY Project\" \/>\n<meta property=\"article:published_time\" content=\"2023-06-15T20:05:00+00:00\" \/>\n<meta property=\"article:modified_time\" content=\"2023-07-21T16:55:14+00:00\" \/>\n<meta property=\"og:image\" content=\"https:\/\/onlyproject.org\/wp-content\/uploads\/2023\/06\/only-watch-only-foundation-1.jpg\" \/>\n\t<meta property=\"og:image:width\" content=\"1400\" \/>\n\t<meta property=\"og:image:height\" content=\"788\" \/>\n\t<meta property=\"og:image:type\" content=\"image\/jpeg\" \/>\n<meta name=\"author\" content=\"andy\" \/>\n<meta name=\"twitter:card\" content=\"summary_large_image\" \/>\n<meta name=\"twitter:label1\" content=\"\u00c9crit par\" \/>\n\t<meta name=\"twitter:data1\" content=\"andy\" \/>\n<script type=\"application\/ld+json\" class=\"yoast-schema-graph\">{\"@context\":\"https:\\\/\\\/schema.org\",\"@graph\":[{\"@type\":\"Article\",\"@id\":\"https:\\\/\\\/onlyproject.org\\\/fr\\\/beginning-of-a-phase-1-clinical-trial-what-to-expect\\\/#article\",\"isPartOf\":{\"@id\":\"https:\\\/\\\/onlyproject.org\\\/fr\\\/beginning-of-a-phase-1-clinical-trial-what-to-expect\\\/\"},\"author\":{\"name\":\"andy\",\"@id\":\"https:\\\/\\\/onlyproject.org\\\/#\\\/schema\\\/person\\\/bb61d9d20f246dedec299e5a13e78d2e\"},\"headline\":\"D\u00e9but de l&rsquo;essai clinique de phase 1 : \u00e0 quoi s&rsquo;attendre ?\",\"datePublished\":\"2023-06-15T20:05:00+00:00\",\"dateModified\":\"2023-07-21T16:55:14+00:00\",\"mainEntityOfPage\":{\"@id\":\"https:\\\/\\\/onlyproject.org\\\/fr\\\/beginning-of-a-phase-1-clinical-trial-what-to-expect\\\/\"},\"wordCount\":11,\"commentCount\":0,\"publisher\":{\"@id\":\"https:\\\/\\\/onlyproject.org\\\/#organization\"},\"image\":{\"@id\":\"https:\\\/\\\/onlyproject.org\\\/fr\\\/beginning-of-a-phase-1-clinical-trial-what-to-expect\\\/#primaryimage\"},\"thumbnailUrl\":\"https:\\\/\\\/onlyproject.org\\\/wp-content\\\/uploads\\\/2023\\\/06\\\/only-watch-only-foundation-1.jpg\",\"articleSection\":[\"Non classifi\u00e9(e)\"],\"inLanguage\":\"fr-FR\",\"potentialAction\":[{\"@type\":\"CommentAction\",\"name\":\"Comment\",\"target\":[\"https:\\\/\\\/onlyproject.org\\\/fr\\\/beginning-of-a-phase-1-clinical-trial-what-to-expect\\\/#respond\"]}]},{\"@type\":\"WebPage\",\"@id\":\"https:\\\/\\\/onlyproject.org\\\/fr\\\/beginning-of-a-phase-1-clinical-trial-what-to-expect\\\/\",\"url\":\"https:\\\/\\\/onlyproject.org\\\/fr\\\/beginning-of-a-phase-1-clinical-trial-what-to-expect\\\/\",\"name\":\"D\u00e9but de l'essai clinique de phase 1 : \u00e0 quoi s'attendre ? 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